Global Pompe Diseases Market Size study, by Route of Administration, By Treatment Type (Substrate Reduction Therapy, Enzyme Replacement Therapy, Chaperone-Advanced Replacement Therapy, Supportive Care), By End User and Regional Forecasts 2022-2028

Description

List of Tables

Global Pompe Diseases Market is valued at approximately USD XXX million in 2021 and is anticipated to grow with a healthy growth rate of more than 4.5% over the forecast period 2022-2028. Pompe disease is a disorder affected by the buildup of a complex sugar called glycogen in the body's cells. It is inherited genetically, and the buildup of glycogen in some tissues and organs, especially muscles, makes them less able to operate normally. In the United States, one in 40,000 people have Pompe disease. The market growth is driven by key factors such as launch of novel drugs and the continued uptake of long-term therapies and increasing development in the field of enzyme replacement therapies. For instance, Enzyme replacement therapy (ERT), which involves giving rhGAA intravenously, is the only treatment for Pompe illness that has been approved, according to a paper titled "Pharmacological Chaperone Therapy for Pompe Disease" that was published in the Journal of Molecules in November 2021. Researchers are looking for novel treatments because of the shortcomings of ERT. which is the sole medication acknowledged by the US Food and Drug Administration. Furthermore, in August 2021, Enzyme Replacement therapy "Aval glucosidase Alfa" has been approved by United State of Food and Drug Administration, for the patient aged 1 year and older with late onset pompe disease. Moreover, emerging immunotherapeutic approaches for Pompe disease create lucrative opportunity for the market in upcoming years. However, high Treatment Cost impedes the growth of the market over the forecast period of 2022-2028

The key regions considered for the global Pompe Diseases Market study include Asia Pacific, North America, Europe, Latin America, and Rest of the World. North America is leading the overall market share owing to rising launches of novel drugs and growing research and development expenditure. However, Asia Pacific is expected to be the fastest growing region due to growing awareness among patients regarding rare disorders and increase in the prevalence of pompe disease in the region.

Major market players included in this report are:

Amicus Therapeutics

CENTOGENE AG

Valerion Therapeutics

Astellas Pharma

EpiVax, Inc

Oxyrane

Sanofi

AVROBIO, Inc.

Genethon

Sangamo Therapeutics

The objective of the study is to define market sizes of different segments & countries in recent years and to forecast the values to the coming eight years. The report is designed to incorporate both qualitative and quantitative aspects of the industry within each of the regions and countries involved in the study. Furthermore, the report also caters the detailed information about the crucial aspects such as driving factors & challenges which will define the future growth of the market. Additionally, the report shall also incorporate available opportunities in micro markets for stakeholders to invest along with the detailed analysis of competitive landscape and Application offerings of key players. The detailed segments and sub-segment of the market are explained below:

By Route of Administration:

Oral

Parenteral

By Treatment Type:

Substrate Reduction Therapy (SRT)

Enzyme Replacement Therapy (ERT)

Chaperone-Advanced Replacement Therapy (CART)

Supportive Care

By End User:

Hospitals

Diagnostic Centers

Ambulatory Surgical Centers

Others

By Region:

North America

U.S.

Canada

Europe

Germany

France

Spain

Italy

ROE

Asia Pacific

China

India

Japan

Australia

South Korea

RoAPAC

Latin America

Brazil

Mexico

Rest of the World

Furthermore, years considered for the study are as follows:

Historical year - 2018, 2019, 2020

Base year - 2021

Forecast period - 2022 to 2028

Target Audience of the Global Pompe Diseases Market in Market Study:

Key Consulting Companies & Advisors

Large, medium-sized, and small enterprises

Venture capitalists

Value-Added Resellers (VARs)

Third-party knowledge providers

Investment bankers

Investors

Chapter 1. Executive Summary

1.1. Market Snapshot
1.2. Global & Segmental Market Estimates & Forecasts, 2020-2028 (USD Million)
- 1.2.1. Pompe Disease Market, by region, 2020-2028 (USD Million)
- 1.2.2. Pompe Disease Market, by Route of Administration, 2020-2028 (USD Million)
- 1.2.3. Pompe Disease Market, by Treatment Type, 2020-2028 (USD Million)
- 1.2.4. Pompe Disease Market, by End User, 2020-2028 (USD Million)
1.3. Key Trends
1.4. Estimation Methodology
1.5. Research Assumption

Chapter 2. Global Pompe Disease Market Definition and Scope

2.1. Objective of the Study
2.2. Market Definition & Scope
- 2.2.1. Scope of the Study
- 2.2.2. Industry Evolution
2.3. Years Considered for the Study
2.4. Currency Conversion Rates

Chapter 3. Global Pompe Disease Market Dynamics

3.1. Pompe Disease Market Impact Analysis (2020-2028)
- 3.1.1. Market Drivers
  - 3.1.1.1. Launch of novel drugs and the continued uptake of long-term therapies
  - 3.1.1.2. Increasing development in the field of enzyme replacement therapies
- 3.1.2. Market Challenges
  - 3.1.2.1. High treatment cost
- 3.1.3. Market Opportunities
  - 3.1.3.1. Emerging immunotherapeutic approaches for Pompe disease

Chapter 4. Global Pompe Disease Market Industry Analysis

4.1. Porter's 5 Force Model
- 4.1.1. Bargaining Power of Suppliers
- 4.1.2. Bargaining Power of Buyers
- 4.1.3. Threat of New Entrants
- 4.1.4. Threat of Substitutes
- 4.1.5. Competitive Rivalry
- 4.1.6. Futuristic Approach to Porter's 5 Force Model (2018-2028)
4.2. PEST Analysis
- 4.2.1. Political
- 4.2.2. Economical
- 4.2.3. Social
- 4.2.4. Technological
4.3. Investment Adoption Model
4.4. Analyst Recommendation & Conclusion
4.5. Top investment opportunity
4.6. Top winning strategies

Chapter 5. Risk Assessment: COVID-19 Impact

5.1.1. Assessment of the overall impact of COVID-19 on the industry
5.1.2. Pre COVID-19 and post COVID-19 market scenario

Chapter 6. Global Pompe Disease Market, by Route of Administration

6.1. Market Snapshot
6.2. Global Pompe Disease Market by Route of Administration, Performance - Potential Analysis
6.3. Global Pompe Disease Market Estimates & Forecasts by Route of Administration, 2018-2028 (USD Million)
6.4. Pompe Disease Market, Sub Segment Analysis
- 6.4.1. Oral
- 6.4.2. Parenteral

Chapter 7. Global Pompe Disease Market, by Treatment Type

7.1. Market Snapshot
7.2. Global Pompe Disease Market by Treatment Type, Performance - Potential Analysis
7.3. Global Pompe Disease Market Estimates & Forecasts by Treatment Type, 2018-2028 (USD Million)
7.4. Pompe Disease Market, Sub Segment Analysis
- 7.4.1. Substrate Reduction Therapy (SRT)
- 7.4.2. Enzyme Replacement Therapy (ERT)
- 7.4.3. Chaperone-Advanced Replacement Therapy (CART)
- 7.4.4. Supportive Care

Chapter 8. Global Pompe Disease Market, by End User

8.1. Market Snapshot
8.2. Global Pompe Disease Market by End User, Performance - Potential Analysis
8.3. Global Pompe Disease Market Estimates & Forecasts by End User, 2018-2028 (USD Million)
8.4. Pompe Disease Market, Sub Segment Analysis
- 8.4.1. Hospitals
- 8.4.2. Diagnostic Centers
- 8.4.3. Ambulatory Surgical Centers
- 8.4.4. Others

Chapter 9. Global Pompe Disease Market, Regional Analysis

9.1. Pompe Disease Market, Regional Market Snapshot
9.2. North America Pompe Disease Market
- 9.2.1. U.S. Pompe Disease Market
  - 9.2.1.1. Route of Administration breakdown estimates & forecasts, 2018-2028
  - 9.2.1.2. Treatment Type breakdown estimates & forecasts, 2018-2028
  - 9.2.1.3. End User breakdown estimates & forecasts, 2018-202
- 9.2.2. Canada Pompe Disease Market
9.3. Europe Pompe Disease Market Snapshot
- 9.3.1. U.K. Pompe Disease Market
- 9.3.2. Germany Pompe Disease Market
- 9.3.3. France Pompe Disease Market
- 9.3.4. Spain Pompe Disease Market
- 9.3.5. Italy Pompe Disease Market
- 9.3.6. Rest of Europe Pompe Disease Market
9.4. Asia-Pacific Pompe Disease Market Snapshot
- 9.4.1. China Pompe Disease Market
- 9.4.2. India Pompe Disease Market
- 9.4.3. Japan Pompe Disease Market
- 9.4.4. Australia Pompe Disease Market
- 9.4.5. South Korea Pompe Disease Market
- 9.4.6. Rest of Asia Pacific Pompe Disease Market
9.5. Latin America Pompe Disease Market Snapshot
- 9.5.1. Brazil Pompe Disease Market
- 9.5.2. Mexico Pompe Disease Market
9.6. Rest of The World Pompe Disease Market

Chapter 10. Competitive Intelligence

10.1. Top Market Strategies
10.2. Company Profiles
- 10.2.1. Sangamo Therapeutics
  - 10.2.1.1. Key Information
  - 10.2.1.2. Overview
  - 10.2.1.3. Financial (Subject to Data Availability)
  - 10.2.1.4. Route of Administration Summary
  - 10.2.1.5. Recent Developments
- 10.2.2. Amicus Therapeutics
- 10.2.3. CENTOGENE AG
- 10.2.4. Valerion Therapeutics
- 10.2.5. Astellas Pharma
- 10.2.6. EpiVax, Inc
- 10.2.7. Oxyrane
- 10.2.8. Sanofi
- 10.2.9. AVROBIO, Inc.
- 10.2.10. Genethon

Chapter 11. Research Process

11.1. Research Process
- 11.1.1. Data Mining
- 11.1.2. Analysis
- 11.1.3. Market Estimation
- 11.1.4. Validation
- 11.1.5. Publishing
11.2. Research Attributes
11.3. Research Assumption

LIST OF TABLES

TABLE 1. Global Pompe Disease Market, report scope
TABLE 2. Global Pompe Disease Market estimates & forecasts by region 2018-2028 (USD Million)
TABLE 3. Global Pompe Disease Market estimates & forecasts by Route of Administration 2018-2028 (USD Million)
TABLE 4. Global Pompe Disease Market estimates & forecasts by Treatment Type 2018-2028 (USD Million)
TABLE 5. Global Pompe Disease Market estimates & forecasts by End User 2018-2028 (USD Million)
TABLE 6.
TABLE 7. Global Pompe Disease Market by segment, estimates & forecasts, 2018-2028 (USD Million)
TABLE 8. Global Pompe Disease Market by region, estimates & forecasts, 2018-2028 (USD Million)
TABLE 9. Global Pompe Disease Market by segment, estimates & forecasts, 2018-2028 (USD Million)
TABLE 10. Global Pompe Disease Market by region, estimates & forecasts, 2018-2028 (USD Million)
TABLE 11. Global Pompe Disease Market by segment, estimates & forecasts, 2018-2028 (USD Million)
TABLE 12. Global Pompe Disease Market by region, estimates & forecasts, 2018-2028 (USD Million)
TABLE 13. Global Pompe Disease Market by segment, estimates & forecasts, 2018-2028 (USD Million)
TABLE 14. Global Pompe Disease Market by region, estimates & forecasts, 2018-2028 (USD Million)
TABLE 15. Global Pompe Disease Market by segment, estimates & forecasts, 2018-2028 (USD Million)
TABLE 16. Global Pompe Disease Market by region, estimates & forecasts, 2018-2028 (USD Million)
TABLE 17. U.S. Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 18. U.S. Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 19. U.S. Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 20. Canada Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 21. Canada Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 22. Canada Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 23. UK Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 24. UK Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 25. UK Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 26. Germany Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 27. Germany Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 28. Germany Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 29. RoE Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 30. RoE Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 31. RoE Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 32. China Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 33. China Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 34. China Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 35. India Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 36. India Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 37. India Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 38. Japan Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 39. Japan Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 40. Japan Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 41. RoAPAC Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 42. RoAPAC Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 43. RoAPAC Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 44. Brazil Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 45. Brazil Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 46. Brazil Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 47. Mexico Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 48. Mexico Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 49. Mexico Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 50. RoLA Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 51. RoLA Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 52. RoLA Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 53. Row Pompe Disease Market estimates & forecasts, 2018-2028 (USD Million)
TABLE 54. Row Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 55. Row Pompe Disease Market estimates & forecasts by segment 2018-2028 (USD Million)
TABLE 56. List of secondary sources, used in the study of global Pompe Disease Market
TABLE 57. List of primary sources, used in the study of global Pompe Disease Market
TABLE 58. Years considered for the study
TABLE 59. Exchange rates considered

LIST OF FIGURES

List of figures

FIG 1. Global Pompe Disease Market, research methodology
FIG 2. Global Pompe Disease Market, market estimation techniques
FIG 3. Global market size estimates & forecast methods
FIG 4. Global Pompe Disease Market, key trends 2021
FIG 5. Global Pompe Disease Market, growth prospects 2022-2028
FIG 6. Global Pompe Disease Market, porters 5 force model
FIG 7. Global Pompe Disease Market, pest analysis
FIG 8. Global Pompe Disease Market, value chain analysis
FIG 9. Global Pompe Disease Market by segment, 2018 & 2028 (USD Million)
FIG 10. Global Pompe Disease Market by segment, 2018 & 2028 (USD Million)
FIG 11. Global Pompe Disease Market by segment, 2018 & 2028 (USD Million)
FIG 12. Global Pompe Disease Market by segment, 2018 & 2028 (USD Million)
FIG 13. Global Pompe Disease Market by segment, 2018 & 2028 (USD Million)
FIG 14. Global Pompe Disease Market, regional snapshot 2018 & 2028
FIG 15. North America Pompe Disease Market 2018 & 2028 (USD Million)
FIG 16. Europe Pompe Disease Market 2018 & 2028 (USD Million)
FIG 17. Asia Pacific Pompe Disease Market 2018 & 2028 (USD Million)
FIG 18. Latin America Pompe Disease Market 2018 & 2028 (USD Million)
FIG 19. Global Pompe Disease Market, company market share analysis (2021)