PUBLISHER: DelveInsight | PRODUCT CODE: 1377965
PUBLISHER: DelveInsight | PRODUCT CODE: 1377965
“"RP-L102 Emerging Drug Insight and Market Forecast - 2032" report provides comprehensive insights about RP-L102 for fanconi anemia in the seven major markets. A detailed picture of the RP-L102 for fanconi anemia in the 7MM, i.e., the United States, EU4 (Germany, France, Italy, and Spain) and the United Kingdom, and Japan for the study period 2019 -2032 is provided in this report along with a detailed description of the RP-L102 for fanconi anemia. The report provides insights about mechanism of action, dosage and administration, as well as research and development including regulatory milestones, along with other developmental activities. Further, it also consists of future market assessments inclusive of the RP-L102 market forecast analysis for fanconi anemia in the 7MM, SWOT, analysts' views, comprehensive overview of market competitors, and brief about other emerging therapies in fanconi anemia.
RP-L102 is a lentiviral vector (LVV)-based gene therapy being developed for the treatment of FA. RP-L102's lentiviral vector carries the FANC-A gene as part of the PGK-FANCA-WPRE expression cassette, which includes a phosphoglycerate kinase (PKG) promoter and an optimized woodchuck hepatitis virus post-transcriptional regulatory element (WPRE). The ex vivo administration process removes and isolates the hematopoietic stem cells using a CD34+ selection process. An autologous genetically modified CD34+ enriched hematopoietic cells (fresh or cryopreserved) are infused into patients to restore function. Further, RP-L102 has been granted OTD, rare pediatric diseases, FTD, and regenerative medicine advanced therapy (RMAT) designations for the treatment of FA type A in the United States and ODD in Europe. Additionally, EMA classified the therapy as an advanced therapy medicinal product (ATMP). It is currently being evaluated in two Phase II trials.
The report provides insights into:
The report is built using data and information sourced primarily from internal databases, primary and secondary research and in-house analysis by DelveInsight's team of industry experts. Information and data from the secondary sources have been obtained from various printable and nonprintable sources like search engines, news websites, global regulatory authorities websites, trade journals, white papers, magazines, books, trade associations, industry associations, industry portals and access to available databases.
RP-L102 Analytical Perspective by DelveInsight
This report provides a detailed market assessment of RP-L102 for fanconi anemia in the seven major markets, i.e., the United States, EU4 (Germany, France, Italy, and Spain) and the United Kingdom, and Japan. This segment of the report provides forecasted sales data from 2024 to 2032.
The report provides the clinical trials information of RP-L102 for fanconi anemia covering trial interventions, trial conditions, trial status, start and completion dates.
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