Global Duchenne Muscular Dystrophy (DMD) Therapeutics Market 2026-2030

Description

The global duchenne muscular dystrophy (dmd) therapeutics market is forecasted to grow by USD 7030.1 mn during 2025-2030, accelerating at a CAGR of 29.4% during the forecast period. The report on the global duchenne muscular dystrophy (dmd) therapeutics market provides a holistic analysis, market size and forecast, trends, growth drivers, and challenges, as well as vendor analysis covering around 25 vendors.

The report offers an up-to-date analysis regarding the current market scenario, the latest trends and drivers, and the overall market environment. The market is driven by commercialization and label expansion of gene therapies, approval of novel non-steroidal and histone deacetylase inhibitors, strategic global partnerships and regulatory progress.

The study was conducted using an objective combination of primary and secondary information including inputs from key participants in the industry. The report contains a comprehensive market size data, segment with regional analysis and vendor landscape in addition to an analysis of the key companies. Reports have historic and forecast data.

Market Scope
Base Year	2026
End Year	2030
Series Year	2026-2030
Growth Momentum	Accelerate
YOY 2026	25.6%
CAGR	29.4%
Incremental Value	$7030.1 mn

Technavio's global duchenne muscular dystrophy (dmd) therapeutics market is segmented as below:

By Type

Biologics
Small molecules

By Distribution Channel

Offline
Online

By Product Type

Corticosteroids
Pain management drugs

Geography

North America
- US
- Canada
- Mexico
Europe
- Germany
- UK
- France
- Italy
- Spain
- The Netherlands
Asia
Rest of World (ROW)
Rest of World (ROW)

This study identifies the expansion of dissociative steroid therapies as one of the prime reasons driving the global duchenne muscular dystrophy (dmd) therapeutics market growth during the next few years. Also, advancement of peptide-conjugated oligonucleotide delivery systems and regulatory trends and innovative treatment adoption will lead to sizable demand in the market.

The report on the global duchenne muscular dystrophy (dmd) therapeutics market covers the following areas:

Global duchenne muscular dystrophy (dmd) therapeutics market sizing
Global duchenne muscular dystrophy (dmd) therapeutics market forecast
Global duchenne muscular dystrophy (dmd) therapeutics market industry analysis

The robust vendor analysis is designed to help clients improve their market position, and in line with this, this report provides a detailed analysis of several leading global duchenne muscular dystrophy (dmd) therapeutics market vendors that include Akashi Therapeutics, Inc., Avidity Biosciences, Inc., BioMarin Pharmaceutical Inc., Capricor Therapeutics Inc., Editas Medicine, Inc., F. Hoffmann La Roche Ltd., FibroGen Inc., Italfarmaco Holding SPA, MeiraGTx Holdings Plc., NS Pharma, Inc., Precision BioSciences, Inc., PTC Therapeutics Inc., ReveraGen BioPharma, Inc., Sarepta Therapeutics Inc., Ultragenyx Pharmaceutical Inc, Wave Life Sciences Ltd.. Also, the global duchenne muscular dystrophy (dmd) therapeutics market analysis report includes information on upcoming trends and challenges that will influence market growth. This is to help companies strategize and leverage all forthcoming growth opportunities.

The publisher presents a detailed picture of the market by the way of study, synthesis, and summation of data from multiple sources by an analysis of key parameters such as profit, pricing, competition, and promotions. It presents various market facets by identifying the key industry influencers. The data presented is comprehensive, reliable, and a result of extensive primary and secondary research. The market research reports provide a complete competitive landscape and an in-depth vendor selection methodology and analysis using qualitative and quantitative research to forecast accurate market growth.

Product Code: IRTNTR71927

1 Executive Summary

1.1 Market overview
- Executive Summary - Chart on Market Overview
- Executive Summary - Data Table on Market Overview
- Executive Summary - Chart on Global Market Characteristics
- Executive Summary - Chart on Market by Geography
- Executive Summary - Chart on Market Segmentation by Type
- Executive Summary - Chart on Market Segmentation by Distribution Channel
- Executive Summary - Chart on Market Segmentation by Product Type
- Executive Summary - Chart on Incremental Growth
- Executive Summary - Data Table on Incremental Growth
- Executive Summary - Chart on Company Market Positioning

2 Technavio Analysis

2.1 Analysis of price sensitivity, lifecycle, customer purchase basket, adoption rates, and purchase criteria
- Analysis of price sensitivity, lifecycle, customer purchase basket, adoption rates, and purchase criteria
2.2 Criticality of inputs and Factors of differentiation
- Chart on Overview on criticality of inputs and factors of differentiation
2.3 Factors of disruption
- Chart on Overview on factors of disruption
2.4 Impact of drivers and challenges
- Chart on Impact of drivers and challenges in 2025 and 2030

3 Market Landscape

3.1 Market ecosystem
- Chart on Parent Market
- Data Table on - Parent Market
3.2 Market characteristics
- Chart on Market characteristics analysis
3.3 Value chain analysis
- Chart on Value chain analysis

4 Market Sizing

4.1 Market definition
- Data Table on Offerings of companies included in the market definition
4.2 Market segment analysis
- Market segments
4.3 Market size 2025
4.4 Market outlook: Forecast for 2025-2030
- Chart on Global - Market size and forecast 2025-2030 ($ million)
- Data Table on Global - Market size and forecast 2025-2030 ($ million)
- Chart on Global Market: Year-over-year growth 2025-2030 (%)
- Data Table on Global Market: Year-over-year growth 2025-2030 (%)

5 Historic Market Size

5.1 Global Duchenne Muscular Dystrophy (DMD) Therapeutics Market 2020 - 2024
- Historic Market Size - Data Table on Global Duchenne Muscular Dystrophy (DMD) Therapeutics Market 2020 - 2024 ($ million)
5.2 Type segment analysis 2020 - 2024
- Historic Market Size - Type Segment 2020 - 2024 ($ million)
5.3 Distribution Channel segment analysis 2020 - 2024
- Historic Market Size - Distribution Channel Segment 2020 - 2024 ($ million)
5.4 Product Type segment analysis 2020 - 2024
- Historic Market Size - Product Type Segment 2020 - 2024 ($ million)
5.5 Geography segment analysis 2020 - 2024
- Historic Market Size - Geography Segment 2020 - 2024 ($ million)
5.6 Country segment analysis 2020 - 2024
- Historic Market Size - Country Segment 2020 - 2024 ($ million)

6 Qualitative Analysis

6.1 Impact of AI in the global duchenne muscular dystrophy (DMD) therapeutics market

7 Five Forces Analysis

7.1 Five forces summary
- Five forces analysis - Comparison between 2025 and 2030
7.2 Bargaining power of buyers
- Bargaining power of buyers - Impact of key factors 2025 and 2030
7.3 Bargaining power of suppliers
- Bargaining power of suppliers - Impact of key factors in 2025 and 2030
7.4 Threat of new entrants
- Threat of new entrants - Impact of key factors in 2025 and 2030
7.5 Threat of substitutes
- Threat of substitutes - Impact of key factors in 2025 and 2030
7.6 Threat of rivalry
- Threat of rivalry - Impact of key factors in 2025 and 2030
7.7 Market condition
- Chart on Market condition - Five forces 2025 and 2030

8 Market Segmentation by Type

8.1 Market segments
- Chart on Type - Market share 2025-2030 (%)
- Data Table on Type - Market share 2025-2030 (%)
8.2 Comparison by Type
- Chart on Comparison by Type
- Data Table on Comparison by Type
8.3 Biologics - Market size and forecast 2025-2030
- Chart on Biologics - Market size and forecast 2025-2030 ($ million)
- Data Table on Biologics - Market size and forecast 2025-2030 ($ million)
- Chart on Biologics - Year-over-year growth 2025-2030 (%)
- Data Table on Biologics - Year-over-year growth 2025-2030 (%)
8.4 Small molecules - Market size and forecast 2025-2030
- Chart on Small molecules - Market size and forecast 2025-2030 ($ million)
- Data Table on Small molecules - Market size and forecast 2025-2030 ($ million)
- Chart on Small molecules - Year-over-year growth 2025-2030 (%)
- Data Table on Small molecules - Year-over-year growth 2025-2030 (%)
8.5 Market opportunity by Type
- Market opportunity by Type ($ million)
- Data Table on Market opportunity by Type ($ million)

9 Market Segmentation by Distribution Channel

9.1 Market segments
- Chart on Distribution Channel - Market share 2025-2030 (%)
- Data Table on Distribution Channel - Market share 2025-2030 (%)
9.2 Comparison by Distribution Channel
- Chart on Comparison by Distribution Channel
- Data Table on Comparison by Distribution Channel
9.3 Offline - Market size and forecast 2025-2030
- Chart on Offline - Market size and forecast 2025-2030 ($ million)
- Data Table on Offline - Market size and forecast 2025-2030 ($ million)
- Chart on Offline - Year-over-year growth 2025-2030 (%)
- Data Table on Offline - Year-over-year growth 2025-2030 (%)
9.4 Online - Market size and forecast 2025-2030
- Chart on Online - Market size and forecast 2025-2030 ($ million)
- Data Table on Online - Market size and forecast 2025-2030 ($ million)
- Chart on Online - Year-over-year growth 2025-2030 (%)
- Data Table on Online - Year-over-year growth 2025-2030 (%)
9.5 Market opportunity by Distribution Channel
- Market opportunity by Distribution Channel ($ million)
- Data Table on Market opportunity by Distribution Channel ($ million)

10 Market Segmentation by Product Type

10.1 Market segments
- Chart on Product Type - Market share 2025-2030 (%)
- Data Table on Product Type - Market share 2025-2030 (%)
10.2 Comparison by Product Type
- Chart on Comparison by Product Type
- Data Table on Comparison by Product Type
10.3 Corticosteroids - Market size and forecast 2025-2030
- Chart on Corticosteroids - Market size and forecast 2025-2030 ($ million)
- Data Table on Corticosteroids - Market size and forecast 2025-2030 ($ million)
- Chart on Corticosteroids - Year-over-year growth 2025-2030 (%)
- Data Table on Corticosteroids - Year-over-year growth 2025-2030 (%)
10.4 Pain management drugs - Market size and forecast 2025-2030
- Chart on Pain management drugs - Market size and forecast 2025-2030 ($ million)
- Data Table on Pain management drugs - Market size and forecast 2025-2030 ($ million)
- Chart on Pain management drugs - Year-over-year growth 2025-2030 (%)
- Data Table on Pain management drugs - Year-over-year growth 2025-2030 (%)
10.5 Market opportunity by Product Type
- Market opportunity by Product Type ($ million)
- Data Table on Market opportunity by Product Type ($ million)

11 Customer Landscape

11.1 Customer landscape overview
- Analysis of price sensitivity, lifecycle, customer purchase basket, adoption rates, and purchase criteria

12 Geographic Landscape

12.1 Geographic segmentation
- Chart on Market share by geography 2025-2030 (%)
- Data Table on Market share by geography 2025-2030 (%)
12.2 Geographic comparison
- Chart on Geographic comparison
- Data Table on Geographic comparison
12.3 North America - Market size and forecast 2025-2030
- Chart on North America - Market size and forecast 2025-2030 ($ million)
- Data Table on North America - Market size and forecast 2025-2030 ($ million)
- Chart on North America - Year-over-year growth 2025-2030 (%)
- Data Table on North America - Year-over-year growth 2025-2030 (%)
- Chart on Regional Comparison - North America
- Data Table on Regional Comparison - North America
- 12.3.1 US - Market size and forecast 2025-2030
  - Chart on US - Market size and forecast 2025-2030 ($ million)
  - Data Table on US - Market size and forecast 2025-2030 ($ million)
  - Chart on US - Year-over-year growth 2025-2030 (%)
  - Data Table on US - Year-over-year growth 2025-2030 (%)
- 12.3.2 Canada - Market size and forecast 2025-2030
  - Chart on Canada - Market size and forecast 2025-2030 ($ million)
  - Data Table on Canada - Market size and forecast 2025-2030 ($ million)
  - Chart on Canada - Year-over-year growth 2025-2030 (%)
  - Data Table on Canada - Year-over-year growth 2025-2030 (%)
- 12.3.3 Mexico - Market size and forecast 2025-2030
  - Chart on Mexico - Market size and forecast 2025-2030 ($ million)
  - Data Table on Mexico - Market size and forecast 2025-2030 ($ million)
  - Chart on Mexico - Year-over-year growth 2025-2030 (%)
  - Data Table on Mexico - Year-over-year growth 2025-2030 (%)
12.4 Europe - Market size and forecast 2025-2030
- Chart on Europe - Market size and forecast 2025-2030 ($ million)
- Data Table on Europe - Market size and forecast 2025-2030 ($ million)
- Chart on Europe - Year-over-year growth 2025-2030 (%)
- Data Table on Europe - Year-over-year growth 2025-2030 (%)
- Chart on Regional Comparison - Europe
- Data Table on Regional Comparison - Europe
- 12.4.1 Germany - Market size and forecast 2025-2030
  - Chart on Germany - Market size and forecast 2025-2030 ($ million)
  - Data Table on Germany - Market size and forecast 2025-2030 ($ million)
  - Chart on Germany - Year-over-year growth 2025-2030 (%)
  - Data Table on Germany - Year-over-year growth 2025-2030 (%)
- 12.4.2 UK - Market size and forecast 2025-2030
  - Chart on UK - Market size and forecast 2025-2030 ($ million)
  - Data Table on UK - Market size and forecast 2025-2030 ($ million)
  - Chart on UK - Year-over-year growth 2025-2030 (%)
  - Data Table on UK - Year-over-year growth 2025-2030 (%)
- 12.4.3 France - Market size and forecast 2025-2030
  - Chart on France - Market size and forecast 2025-2030 ($ million)
  - Data Table on France - Market size and forecast 2025-2030 ($ million)
  - Chart on France - Year-over-year growth 2025-2030 (%)
  - Data Table on France - Year-over-year growth 2025-2030 (%)
- 12.4.4 Italy - Market size and forecast 2025-2030
  - Chart on Italy - Market size and forecast 2025-2030 ($ million)
  - Data Table on Italy - Market size and forecast 2025-2030 ($ million)
  - Chart on Italy - Year-over-year growth 2025-2030 (%)
  - Data Table on Italy - Year-over-year growth 2025-2030 (%)
- 12.4.5 Spain - Market size and forecast 2025-2030
  - Chart on Spain - Market size and forecast 2025-2030 ($ million)
  - Data Table on Spain - Market size and forecast 2025-2030 ($ million)
  - Chart on Spain - Year-over-year growth 2025-2030 (%)
  - Data Table on Spain - Year-over-year growth 2025-2030 (%)
- 12.4.6 The Netherlands - Market size and forecast 2025-2030
  - Chart on The Netherlands - Market size and forecast 2025-2030 ($ million)
  - Data Table on The Netherlands - Market size and forecast 2025-2030 ($ million)
  - Chart on The Netherlands - Year-over-year growth 2025-2030 (%)
  - Data Table on The Netherlands - Year-over-year growth 2025-2030 (%)
12.5 Asia - Market size and forecast 2025-2030
- Chart on Asia - Market size and forecast 2025-2030 ($ million)
- Data Table on Asia - Market size and forecast 2025-2030 ($ million)
- Chart on Asia - Year-over-year growth 2025-2030 (%)
- Data Table on Asia - Year-over-year growth 2025-2030 (%)
- Chart on Regional Comparison - Asia
- Data Table on Regional Comparison - Asia
- 12.5.1 China - Market size and forecast 2025-2030
  - Chart on China - Market size and forecast 2025-2030 ($ million)
  - Data Table on China - Market size and forecast 2025-2030 ($ million)
  - Chart on China - Year-over-year growth 2025-2030 (%)
  - Data Table on China - Year-over-year growth 2025-2030 (%)
- 12.5.2 Japan - Market size and forecast 2025-2030
  - Chart on Japan - Market size and forecast 2025-2030 ($ million)
  - Data Table on Japan - Market size and forecast 2025-2030 ($ million)
  - Chart on Japan - Year-over-year growth 2025-2030 (%)
  - Data Table on Japan - Year-over-year growth 2025-2030 (%)
- 12.5.3 India - Market size and forecast 2025-2030
  - Chart on India - Market size and forecast 2025-2030 ($ million)
  - Data Table on India - Market size and forecast 2025-2030 ($ million)
  - Chart on India - Year-over-year growth 2025-2030 (%)
  - Data Table on India - Year-over-year growth 2025-2030 (%)
- 12.5.4 South Korea - Market size and forecast 2025-2030
  - Chart on South Korea - Market size and forecast 2025-2030 ($ million)
  - Data Table on South Korea - Market size and forecast 2025-2030 ($ million)
  - Chart on South Korea - Year-over-year growth 2025-2030 (%)
  - Data Table on South Korea - Year-over-year growth 2025-2030 (%)
- 12.5.5 Indonesia - Market size and forecast 2025-2030
  - Chart on Indonesia - Market size and forecast 2025-2030 ($ million)
  - Data Table on Indonesia - Market size and forecast 2025-2030 ($ million)
  - Chart on Indonesia - Year-over-year growth 2025-2030 (%)
  - Data Table on Indonesia - Year-over-year growth 2025-2030 (%)
- 12.5.6 Thailand - Market size and forecast 2025-2030
- Chart on Thailand - Market size and forecast 2025-2030 ($ million)
- Data Table on Thailand - Market size and forecast 2025-2030 ($ million)
- Chart on Thailand - Year-over-year growth 2025-2030 (%)
- Data Table on Thailand - Year-over-year growth 2025-2030 (%)
12.6 Rest of World (ROW) - Market size and forecast 2025-2030
- Chart on Rest of World (ROW) - Market size and forecast 2025-2030 ($ million)
- Data Table on Rest of World (ROW) - Market size and forecast 2025-2030 ($ million)
- Chart on Rest of World (ROW) - Year-over-year growth 2025-2030 (%)
- Data Table on Rest of World (ROW) - Year-over-year growth 2025-2030 (%)
- Chart on Regional Comparison - Rest of World (ROW)
- Data Table on Regional Comparison - Rest of World (ROW)
- 12.6.1 Brazil - Market size and forecast 2025-2030
  - Chart on Brazil - Market size and forecast 2025-2030 ($ million)
  - Data Table on Brazil - Market size and forecast 2025-2030 ($ million)
  - Chart on Brazil - Year-over-year growth 2025-2030 (%)
  - Data Table on Brazil - Year-over-year growth 2025-2030 (%)
- 12.6.2 South Africa - Market size and forecast 2025-2030
  - Chart on South Africa - Market size and forecast 2025-2030 ($ million)
  - Data Table on South Africa - Market size and forecast 2025-2030 ($ million)
  - Chart on South Africa - Year-over-year growth 2025-2030 (%)
  - Data Table on South Africa - Year-over-year growth 2025-2030 (%)
- 12.6.3 Australia - Market size and forecast 2025-2030
  - Chart on Australia - Market size and forecast 2025-2030 ($ million)
  - Data Table on Australia - Market size and forecast 2025-2030 ($ million)
  - Chart on Australia - Year-over-year growth 2025-2030 (%)
  - Data Table on Australia - Year-over-year growth 2025-2030 (%)
- 12.6.4 Argentina - Market size and forecast 2025-2030
  - Chart on Argentina - Market size and forecast 2025-2030 ($ million)
  - Data Table on Argentina - Market size and forecast 2025-2030 ($ million)
  - Chart on Argentina - Year-over-year growth 2025-2030 (%)
  - Data Table on Argentina - Year-over-year growth 2025-2030 (%)
- 12.6.5 Saudi Arabia - Market size and forecast 2025-2030
  - Chart on Saudi Arabia - Market size and forecast 2025-2030 ($ million)
  - Data Table on Saudi Arabia - Market size and forecast 2025-2030 ($ million)
  - Chart on Saudi Arabia - Year-over-year growth 2025-2030 (%)
  - Data Table on Saudi Arabia - Year-over-year growth 2025-2030 (%)
- 12.6.6 Nigeria - Market size and forecast 2025-2030
- Chart on Nigeria - Market size and forecast 2025-2030 ($ million)
- Data Table on Nigeria - Market size and forecast 2025-2030 ($ million)
- Chart on Nigeria - Year-over-year growth 2025-2030 (%)
- Data Table on Nigeria - Year-over-year growth 2025-2030 (%)
- 12.6.7 UAE - Market size and forecast 2025-2030
  - Chart on UAE - Market size and forecast 2025-2030 ($ million)
  - Data Table on UAE - Market size and forecast 2025-2030 ($ million)
  - Chart on UAE - Year-over-year growth 2025-2030 (%)
  - Data Table on UAE - Year-over-year growth 2025-2030 (%)
- 12.6.8 Colombia - Market size and forecast 2025-2030
- Chart on Colombia - Market size and forecast 2025-2030 ($ million)
- Data Table on Colombia - Market size and forecast 2025-2030 ($ million)
- Chart on Colombia - Year-over-year growth 2025-2030 (%)
- Data Table on Colombia - Year-over-year growth 2025-2030 (%)
12.7 Market opportunity by geography
- Market opportunity by geography ($ million)
- Data Tables on Market opportunity by geography ($ million)

13 Drivers, Challenges, and Opportunity

13.1 Market drivers
- Commercialization and label expansion of gene therapies
- Approval of novel non-steroidal and histone deacetylase inhibitors
- Strategic global partnerships and regulatory progress
13.2 Market challenges
- High cost of treatment and reimbursement barriers
- Regulatory divergence and stringent efficacy standards
- Clinical trial failures and scientific complexity
13.3 Impact of drivers and challenges
- Impact of drivers and challenges in 2025 and 2030
13.4 Market opportunities
- Expansion of dissociative steroid therapies
- Advancement of peptide-conjugated oligonucleotide delivery systems
- Regulatory trends and innovative treatment adoption

14 Competitive Landscape

14.1 Overview
14.2 Competitive Landscape
- Overview on criticality of inputs and factors of differentiation
14.3 Landscape disruption
- Overview on factors of disruption
14.4 Industry risks
- Impact of key risks on business

15 Competitive Analysis

15.1 Companies profiled
- Companies covered
15.2 Company ranking index
- Company ranking index
15.3 Market positioning of companies
- Matrix on companies position and classification
15.4 Akashi Therapeutics, Inc.
- Akashi Therapeutics, Inc. - Overview
- Akashi Therapeutics, Inc. - Product / Service
- Akashi Therapeutics, Inc. - Key offerings
- SWOT
15.5 Avidity Biosciences, Inc.
- Avidity Biosciences, Inc. - Overview
- Avidity Biosciences, Inc. - Product / Service
- Avidity Biosciences, Inc. - Key offerings
- SWOT
15.6 BioMarin Pharmaceutical Inc.
- BioMarin Pharmaceutical Inc. - Overview
- BioMarin Pharmaceutical Inc. - Product / Service
- BioMarin Pharmaceutical Inc. - Key offerings
- SWOT
15.7 Capricor Therapeutics Inc.
- Capricor Therapeutics Inc. - Overview
- Capricor Therapeutics Inc. - Product / Service
- Capricor Therapeutics Inc. - Key offerings
- SWOT
15.8 F. Hoffmann La Roche Ltd.
- F. Hoffmann La Roche Ltd. - Overview
- F. Hoffmann La Roche Ltd. - Business segments
- F. Hoffmann La Roche Ltd. - Key news
- F. Hoffmann La Roche Ltd. - Key offerings
- F. Hoffmann La Roche Ltd. - Segment focus
- SWOT
15.9 FibroGen Inc.
- FibroGen Inc. - Overview
- FibroGen Inc. - Product / Service
- FibroGen Inc. - Key offerings
- SWOT
15.10 Italfarmaco Holding SPA
- Italfarmaco Holding SPA - Overview
- Italfarmaco Holding SPA - Product / Service
- Italfarmaco Holding SPA - Key offerings
- SWOT
15.11 MeiraGTx Holdings Plc.
- MeiraGTx Holdings Plc. - Overview
- MeiraGTx Holdings Plc. - Product / Service
- MeiraGTx Holdings Plc. - Key offerings
- SWOT
15.12 NS Pharma, Inc.
- NS Pharma, Inc. - Overview
- NS Pharma, Inc. - Product / Service
- NS Pharma, Inc. - Key offerings
- SWOT
15.13 Precision BioSciences, Inc.
- Precision BioSciences, Inc. - Overview
- Precision BioSciences, Inc. - Product / Service
- Precision BioSciences, Inc. - Key offerings
- SWOT
15.14 PTC Therapeutics Inc.
- PTC Therapeutics Inc. - Overview
- PTC Therapeutics Inc. - Product / Service
- PTC Therapeutics Inc. - Key offerings
- SWOT
15.15 ReveraGen BioPharma, Inc.
- ReveraGen BioPharma, Inc. - Overview
- ReveraGen BioPharma, Inc. - Product / Service
- ReveraGen BioPharma, Inc. - Key offerings
- SWOT
15.16 Sarepta Therapeutics Inc.
- Sarepta Therapeutics Inc. - Overview
- Sarepta Therapeutics Inc. - Product / Service
- Sarepta Therapeutics Inc. - Key offerings
- SWOT
15.17 Ultragenyx Pharmaceutical Inc
- Ultragenyx Pharmaceutical Inc - Overview
- Ultragenyx Pharmaceutical Inc - Product / Service
- Ultragenyx Pharmaceutical Inc - Key offerings
- SWOT
15.18 Wave Life Sciences Ltd.
- Wave Life Sciences Ltd. - Overview
- Wave Life Sciences Ltd. - Product / Service
- Wave Life Sciences Ltd. - Key offerings
- SWOT

16 Appendix

16.1 Scope of the report
- Market definition
- Objectives
- Notes and caveats
16.2 Inclusions and exclusions checklist
- Inclusions checklist
- Exclusions checklist
16.3 Currency conversion rates for US$
- Currency conversion rates for US$
16.4 Research methodology
- Research methodology
16.5 Data procurement
- Information sources
16.6 Data validation
- Data validation
16.7 Validation techniques employed for market sizing
- Validation techniques employed for market sizing
16.8 Data synthesis
- Data synthesis
16.9 360 degree market analysis
- 360 degree market analysis
16.10 List of abbreviations
- List of abbreviations