The global Gene Therapy R&D market is projected to grow at a CAGR of 30.9% by 2035.
The Gene Therapy R&D Market Report 2025-2035 (Including Impact of U.S. Trade Tariffs): This report will prove invaluable to leading firms striving for new revenue pockets if they wish to better understand the industry and its underlying dynamics. It will be useful for companies that would like to expand into different industries or to expand their existing operations in a new region.
Robust Gene Therapy Pipeline to Boost Growth
Cell and gene therapies (CGTs) are increasingly moving from the research labs to the clinic, owing to the fact that they target particular disease rather than the limited targets of small-molecule therapies. Both methods of therapy aim to introduce healthy cells or correct genetic defects in patients. Cancer is the primary area of interest and nearly half of all cell & gene therapies in clinical trials. CAR-T therapy (Chimeric Antigen Receptors), which combines cell & gene therapy, is one promising cancer treatment. CAR-T therapy takes a patient's immune cells and modifies their DNA to make them respond against cancer cells. The patient's immune system is reintroduced with modified gene cells, allowing immune system to battle the cancer.
The FDA has already given its approval to two CAR-T therapies. When no other treatment options were working, these therapies benefited some cancer patients. With further research activities, these therapies may become more widely available & capable of treating a wider variety of cancers. The registered clinical trials in Q1 2025 were reported to be 2,155 as compared to 2,093 in Q1 2024. Oncology and rare diseases remained the top areas of gene therapy development in both the overall pipeline (preclinical to pre-registration) and in the clinic (Phase I to pre-registration)
Development for rare diseases most commonly occurred in oncology, representing a majority of 52% compared to non-oncology rare disease gene therapy pipeline development
What would be the Impact of US Trade Tariffs on the Global Gene Therapy R&D Market?
The recent expansion of U.S. trade tariffs on pharmaceutical and biotechnological imports is expected to increase operational costs for gene therapy developers. As many critical materials, reagents, and specialised instruments used in R&D are sourced internationally, these tariffs could lead to supply chain disruptions, longer lead times, and higher procurement expenses. Smaller research organisations and academic groups may be most affected, as they have limited flexibility to absorb additional costs. Over time, this may encourage greater localisation of production, as companies seek to mitigate exposure to tariff risks by establishing domestic manufacturing and sourcing capabilities. While such measures could strengthen regional resilience, they also risk fragmenting global collaboration networks that have been vital to innovation in gene therapy research and development.
What Questions Should You Ask before Buying a Market Research Report?
- How is the gene therapy R&D market evolving?
- What is driving and restraining the gene therapy R&D market?
- How will each gene therapy R&D submarket segment grow over the forecast period and how much revenue will these submarkets account for in 2035?
- How will the market shares for each gene therapy R&D submarket develop from 2025 to 2035?
- What will be the main driver for the overall market from 2025 to 2035?
- Will leading gene therapy R&D markets broadly follow the macroeconomic dynamics, or will individual national markets outperform others?
- How will the market shares of the national markets change by 2035 and which geographical region will lead the market in 2035?
- Who are the leading players and what are their prospects over the forecast period?
- What are the gene therapy R&D projects for these leading companies?
- How will the industry evolve during the period between 2025 and 2035? What are the implications of
- gene therapy R&D projects taking place now and over the next 10 years?
- Is there a greater need for product commercialisation to further scale the gene therapy R&D market?
- Where is the gene therapy R&D market heading and how can you ensure you are at the forefront of the market?
- What are the best investment options for new product and service lines?
- What are the key prospects for moving companies into a new growth path and C-suite?
You need to discover how this will impact the Gene Therapy R&D market today, and over the next 10 years:
- Our 357-page report provides 155 tables and 185 charts/graphs exclusively to you.
- The report highlights key lucrative areas in the industry so you can target them - NOW.
- It contains in-depth analysis of global, regional and national sales and growth.
- It highlights for you the key successful trends, changes and revenue projections made by your competitors.
- Forecasts to 2035 and other analyses reveal commercial prospects
- In addition to revenue forecasting to 2035, our new study provides you with recent results, growth rates, and market shares.
- You will find original analyses, with business outlooks and developments.
- Discover qualitative analyses (including market dynamics, drivers, opportunities, and restraints), Porter's Five Forces Analysis, PEST Analysis and recent developments.
Segments Covered in the Report
- Disease
- Cancer
- Rare Diseases
- Cardiovascular Diseases
- Ophthalmic Diseases
- Haematology
- Neurological
- Diabetes Mellitus
- Other Diseases
- Vector
- Viral
- Retrovirus
- Adenovirus
- AAV
- Lentivirus
- Others
- Non-viral
- Naked DNA
- Gene Gun
- Electroporation
- Lipofection
- Techniques
- Gene Augmentation Therapy
- Gene Replacement Therapy
- Participants
- Small/Medium Pharma & Biotech
- Universities & Research Institutes
- Hospitals, Government & Public Bodies
- Big Pharma
In addition to the revenue predictions for the overall world market and segments, you will also find revenue forecasts for five regional and 22 leading national markets:
- North America
- U.S.
- Canada
- Europe
- Germany
- UK
- France
- Italy
- Spain
- Russia
- Rest of Europe
- Asia Pacific
- Japan
- China
- India
- Australia
- South Korea
- South East Asia
- Rest of Asia Pacific
- Latin America
- Brazil
- Mexico
- Rest of Latin America
- MEA
- GCC
- South Africa
- Rest of MEA
The report also includes profiles for some of the leading companies in the Gene Therapy R&D Market, 2025 to 2035, with a focus on this segment of these companies' operations.
- Leading companies and the potential for market growth
- American Gene Technologies
- Applied Genetic
- Astellas Pharma Inc.
- Bayer
- Benitec BioPharma
- Biogen
- Bluebird Bio
- Bristol Myers Squibb
- Calimmune, Inc. (CSL Behiring)
- Cellectis
- GenSight Biologics
- Gilead Lifesciences, Inc.
- GQ Bio Therapeutics GmbH (Pacira Pharmaceuticals, Inc.)
- Novartis AG
- OCUGEN, INC.
- Orchard Therapeutics
- Oxford Biomedica
- Pfizer, Inc.
- REGENXBIO Inc.
- Sangamo Therapeutics, Inc.
- Sanofi
- Sarepta Therapeutics, Inc.
- Spark Therapeutics (Subsidiary of Roche)
- Takeda Pharmaceutical Company Limited
- Taysha GTx
- Transgene
- UniQure N. V.
- VeonGen Therapeutics
- Voyager Therapeutics Inc.
Overall world revenue for Gene Therapy R&D Market, 2025 to 2035 in terms of value the market will surpass US$3,500 million in 2025, our work calculates. We predict strong revenue growth through to 2035. Our work identifies which organizations hold the greatest potential. Discover their capabilities, progress, and commercial prospects, helping you stay ahead.
- How will the Gene Therapy R&D Market, 2025 to 2035 report help you?
- In summary, our 350+ page report provides you with the following knowledge:
- Revenue forecasts to 2035 for Gene Therapy R&D Market 2025 to 2035, with forecasts for Disease, Vector, Techniques, and Participants, each forecast at a global and regional level - discover the industry's prospects, finding the most lucrative places for investments and revenues.
- Revenue forecasts to 2035 for five regional and 22 key national markets - See forecasts for the Gene Therapy R&D Market, 2025 to 2035 market in North America, Europe, Asia-Pacific, Latin America, and MEA. Also forecasted is the market in the US, Canada, Mexico, Brazil, Germany, France, UK, Italy, China, India, Japan, and Australia among other prominent economies.
- Prospects for established firms and those seeking to enter the market - including company profiles for 29 of the major companies involved in the Gene Therapy R&D Market, 2025 to 2035.
- Find quantitative and qualitative analyses with independent predictions. Receive information that only our report contains, staying informed with invaluable business intelligence.
- Information found nowhere else
- With our new report, you are less likely to fall behind in knowledge or miss out on opportunities. See how our work could benefit your research, analyses, and decisions. Visiongain's study is for everybody needing commercial analyses for the Gene Therapy R&D Market 2025 to 2035, market-leading companies. You will find data, trends and predictions.