Gene Therapy For Inherited Genetic Disorders Global Market Report 2025

Description

Gene therapy for inherited genetic disorders is a medical approach that addresses the underlying cause of hereditary diseases by repairing or replacing defective genes. Its primary objective is to provide a potential cure rather than merely managing symptoms. By introducing functional genes into a patient's cells, it restores normal cellular function and improves overall health. This strategy holds significant potential for treating rare genetic disorders, offering the possibility of long-lasting or permanent therapeutic benefits.

The primary types of gene therapy for inherited genetic disorders include viral vector-based therapies, gene editing techniques, RNA-based therapies, and ex vivo gene therapy. Viral vector-based therapies employ genetically modified, non-replicating viruses to deliver therapeutic genetic material into patient cells to treat diseases. These therapies are utilized in various applications, including inherited metabolic disorders, neurological disorders, cardiovascular disorders, musculoskeletal disorders, and ophthalmic disorders, and serve multiple end users such as hospitals, specialty clinics, research institutions, and others.

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report's Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

The sudden escalation of U.S. tariffs and the consequent trade frictions in spring 2025 are severely impacting the pharmaceutical companies contend with tariffs on APIs, glass vials, and lab equipment inputs with few alternative sources. Generic drug makers, operating on razor-thin margins, are especially vulnerable, with some reducing production of low-profit medicines. Biotech firms face delays in clinical trials due to tariff-related shortages of specialized reagents. In response, the industry is expanding API production in India and Europe, increasing inventory stockpiles, and pushing for trade exemptions for essential medicines.

The gene therapy for inherited genetic disorders market research report is one of a series of new reports from The Business Research Company that provides gene therapy for inherited genetic disorders market statistics, including gene therapy for inherited genetic disorders industry global market size, regional shares, competitors with a gene therapy for inherited genetic disorders market share, detailed gene therapy for inherited genetic disorders market segments, market trends and opportunities, and any further data you may need to thrive in the gene therapy for inherited genetic disorders industry. This gene therapy for inherited genetic disorders market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenario of the industry.

The gene therapy for inherited genetic disorders market size has grown rapidly in recent years. It will grow from $3.39 billion in 2024 to $4.05 billion in 2025 at a compound annual growth rate (CAGR) of 19.4%. The growth in the historic period can be attributed to rising government initiatives and supportive policies for gene therapy, expanding availability of advanced gene delivery systems, increasing patient demand for effective and curative treatments, the growth of clinical trials targeting inherited disorders, and heightened awareness among healthcare professionals about the benefits of gene therapy.

The gene therapy for inherited genetic disorders market size is expected to see rapid growth in the next few years. It will grow to $8.15 billion in 2029 at a compound annual growth rate (CAGR) of 19.1%. The growth in the forecast period can be attributed to the rising prevalence of inherited genetic disorders, increasing investment and funding in gene therapy research and development, greater awareness and diagnosis of rare genetic diseases, growing regulatory approvals for novel gene therapy products, and expanding adoption of personalized medicine approaches. Major trends in the forecast period include the integration of advanced delivery systems for targeted gene therapy, innovations in viral and non-viral vector technologies, advancements in next-generation sequencing for precise diagnosis, improvements in manufacturing and scalability of gene therapies, and the use of artificial intelligence to optimize gene therapy design.

The rising demand for personalized medicine is anticipated to drive the growth of the gene therapy for inherited genetic disorders market in the coming years. Personalized medicine involves tailoring medical treatments to an individual's genetic profile and personal characteristics to optimize care. This approach is gaining momentum due to advancements in genetic technologies, which make it easier and more cost-effective to customize treatments according to a person's unique genetic makeup. Personalized medicine enhances gene therapy by enabling precise gene targeting and delivery, improving treatment effectiveness, and reducing side effects. For example, in February 2024, the Personalized Medicine Coalition, a US-based non-profit organization, reported that the US Food and Drug Administration (FDA) approved 16 new personalized treatments for rare disease patients in 2023, up from six in 2022. These newly approved treatments included seven cancer drugs and three for other diseases and conditions. Consequently, the growing demand for personalized medicine is fueling the expansion of the gene therapy for inherited genetic disorders market.

Leading companies in the gene therapy for inherited genetic disorders market are focusing on developing advanced solutions, such as gene therapy establishments, to create targeted, safer, and more effective treatments that address the root causes of genetic diseases. A gene therapy establishment is a biotechnology or pharmaceutical company specializing in researching, developing, and commercializing gene therapies aimed at correcting or modifying defective genes responsible for inherited genetic disorders. For instance, in November 2022, Replay, a US-based genome-writing company, launched Telaria, a major DNA HSV gene therapy company. Telaria is the second product company utilizing Replay's high-payload herpes simplex virus (HSV) delivery vector, synHSV, with its lead indication targeting recessive dystrophic epidermolysis bullosa (RDEB), a severe genetic skin disorder. The company was co-founded by leading HSV scientists and genetic skin disease experts, aiming to develop transformative gene therapies for rare skin conditions. This launch followed Replay's first gene therapy company, Eudora, which focuses on retinal diseases. Replay's innovative structure separates technology development from therapeutic development within distinct product companies focused on specific disease areas.

In October 2024, Ocuphire Pharma Inc., a US-based biotechnology company, acquired Opus Genetics Inc. for an undisclosed amount. Through this acquisition, Ocuphire Pharma aims to become a leader in developing and advancing gene therapies for rare inherited retinal diseases by combining Opus's innovative pipeline with its own development expertise. Opus Genetics Inc., also a US-based biotechnology company, specializes in gene therapy for inherited genetic disorders.

Major players in the gene therapy for inherited genetic disorders market are Sanofi S.A., Novartis AG, Astellas Pharma Inc., Vertex Pharmaceuticals Incorporated, Genentech, Biomarin Pharmaceutical Inc, Sarepta Therapeutics Inc., Krystal Biotech Inc., Rocket Pharmaceuticals Inc., Sangamo Therapeutics Inc., REGENXBIO Inc., Passage Bio Inc., Voyager Therapeutics Inc., Generation Bio Co., Avrobio Inc, Editas Medicine Inc., MeiraGTx Holdings Plc, uniQure N.V., Intellia Therapeutics Inc., Bluebird Bio Inc, 4D Molecular Therapeutics Inc., CRISPR Therapeutics AG.

North America was the largest region in the gene therapy for inherited genetic disorders market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in gene therapy for inherited genetic disorders market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The countries covered in the gene therapy for inherited genetic disorders market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

The gene therapy for inherited genetic disorders market consists of revenues earned by entities by providing services such as genetic testing and diagnosis, personalized treatment planning, and gene delivery and administration. The market value includes the value of related goods sold by the service provider or included within the service offering. The gene therapy for inherited genetic disorders market also includes sales of zolgensma, luxturna, and strimvelis. Values in this market are 'factory gate' values, that is, the value of goods sold by the manufacturers or creators of the goods, whether to other entities (including downstream manufacturers, wholesalers, distributors, and retailers) or directly to end customers. The value of goods in this market includes related services sold by the creators of the goods.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

Gene Therapy For Inherited Genetic Disorders Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on gene therapy for inherited genetic disorders market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

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Where is the largest and fastest growing market for gene therapy for inherited genetic disorders ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward, including technological disruption, regulatory shifts, and changing consumer preferences? The gene therapy for inherited genetic disorders market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

The market characteristics section of the report defines and explains the market.
The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
The forecasts are made after considering the major factors currently impacting the market. These include:

The forecasts are made after considering the major factors currently impacting the market. These include the technological advancements such as AI and automation, Russia-Ukraine war, trade tariffs (government-imposed import/export duties), elevated inflation and interest rates.

Market segmentations break down the market into sub markets.
The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth.
The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.

Scope

Markets Covered:1) By Type: Viral Vector-Based Therapies; Gene Editing Techniques; Ribonucleic Acid-Based Therapies; Ex Vivo Gene Therapy
2) By Application: Inherited Metabolic Disorders; Neurological Disorders; Cardiovascular Disorders; Musculoskeletal Disorders; Ophthalmic Disorders
3) By End-User: Hospitals; Specialty Clinics; Research Institutes; Other End-Users
Subsegments:
1) By Viral Vector-Based Therapies: Adenovirus Vectors; Adeno-Associated Virus (AAV) Vectors; Lentivirus Vectors
2) By Gene Editing Techniques: Zinc Finger Nucleases (ZFNs); Transcription Activator-Like Effector Nucleases (TALENs); Meganucleases
3) By Ribonucleic Acid-Based Therapies: Small Interfering Ribonucleic Acid; Antisense Oligonucleotides (ASOs); Messenger Ribonucleic Acid (mRNA) Therapies
4) By Ex Vivo Gene Therapy: Hematopoietic Stem Cell Gene Therapy; Mesenchymal Stem Cell Gene Therapy; Induced Pluripotent Stem Cell (iPSC) Therapy
Companies Mentioned: Sanofi S.A.; Novartis AG; Astellas Pharma Inc.; Vertex Pharmaceuticals Incorporated; Genentech; Biomarin Pharmaceutical Inc; Sarepta Therapeutics Inc.; Krystal Biotech Inc.; Rocket Pharmaceuticals Inc.; Sangamo Therapeutics Inc.; REGENXBIO Inc.; Passage Bio Inc.; Voyager Therapeutics Inc.; Generation Bio Co.; Avrobio Inc; Editas Medicine Inc.; MeiraGTx Holdings Plc; uniQure N.V.; Intellia Therapeutics Inc.; Bluebird Bio Inc; 4D Molecular Therapeutics Inc.; CRISPR Therapeutics AG
Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain
Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa
Time Series: Five years historic and ten years forecast.
Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,
Data Segmentations: country and regional historic and forecast data, market share of competitors, market segments.
Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.
Delivery Format: PDF, Word and Excel Data Dashboard.

Product Code: r37764

1. Executive Summary

2. Gene Therapy For Inherited Genetic Disorders Market Characteristics

3. Gene Therapy For Inherited Genetic Disorders Market Trends And Strategies

4. Gene Therapy For Inherited Genetic Disorders Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

4.1. Supply Chain Impact from Tariff War & Trade Protectionism

5. Global Gene Therapy For Inherited Genetic Disorders Growth Analysis And Strategic Analysis Framework

5.1. Global Gene Therapy For Inherited Genetic Disorders PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
5.2. Analysis Of End Use Industries
5.3. Global Gene Therapy For Inherited Genetic Disorders Market Growth Rate Analysis
5.4. Global Gene Therapy For Inherited Genetic Disorders Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
5.5. Global Gene Therapy For Inherited Genetic Disorders Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
5.6. Global Gene Therapy For Inherited Genetic Disorders Total Addressable Market (TAM)

6. Gene Therapy For Inherited Genetic Disorders Market Segmentation

6.1. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Viral Vector-Based Therapies
Gene Editing Techniques
Ribonucleic Acid-Based Therapies
Ex Vivo Gene Therapy
6.2. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Inherited Metabolic Disorders
Neurological Disorders
Cardiovascular Disorders
Musculoskeletal Disorders
Ophthalmic Disorders
6.3. Global Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hospitals
Specialty Clinics
Research Institutes
Other End-Users
6.4. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Viral Vector-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Adenovirus Vectors
Adeno-Associated Virus (AAV) Vectors
Lentivirus Vectors
6.5. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Gene Editing Techniques, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Zinc Finger Nucleases (ZFNs)
Transcription Activator-Like Effector Nucleases (TALENs)
Meganucleases
6.6. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ribonucleic Acid-Based Therapies, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Small Interfering Ribonucleic Acid
Antisense Oligonucleotides (ASOs)
Messenger Ribonucleic Acid (mRNA) Therapies
6.7. Global Gene Therapy For Inherited Genetic Disorders Market, Sub-Segmentation Of Ex Vivo Gene Therapy, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hematopoietic Stem Cell Gene Therapy
Mesenchymal Stem Cell Gene Therapy
Induced Pluripotent Stem Cell (iPSC) Therapy

7. Gene Therapy For Inherited Genetic Disorders Market Regional And Country Analysis

7.1. Global Gene Therapy For Inherited Genetic Disorders Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
7.2. Global Gene Therapy For Inherited Genetic Disorders Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market

8.1. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market Overview
Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
8.2. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.3. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.4. Asia-Pacific Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

9. China Gene Therapy For Inherited Genetic Disorders Market

9.1. China Gene Therapy For Inherited Genetic Disorders Market Overview
9.2. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.3. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.4. China Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

10. India Gene Therapy For Inherited Genetic Disorders Market

10.1. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.2. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.3. India Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11. Japan Gene Therapy For Inherited Genetic Disorders Market

11.1. Japan Gene Therapy For Inherited Genetic Disorders Market Overview
11.2. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.3. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.4. Japan Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12. Australia Gene Therapy For Inherited Genetic Disorders Market

12.1. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.2. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.3. Australia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13. Indonesia Gene Therapy For Inherited Genetic Disorders Market

13.1. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.2. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.3. Indonesia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14. South Korea Gene Therapy For Inherited Genetic Disorders Market

14.1. South Korea Gene Therapy For Inherited Genetic Disorders Market Overview
14.2. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.3. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.4. South Korea Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15. Western Europe Gene Therapy For Inherited Genetic Disorders Market

15.1. Western Europe Gene Therapy For Inherited Genetic Disorders Market Overview
15.2. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.3. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.4. Western Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16. UK Gene Therapy For Inherited Genetic Disorders Market

16.1. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.2. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.3. UK Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17. Germany Gene Therapy For Inherited Genetic Disorders Market

17.1. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.2. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.3. Germany Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18. France Gene Therapy For Inherited Genetic Disorders Market

18.1. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.2. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.3. France Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19. Italy Gene Therapy For Inherited Genetic Disorders Market

19.1. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.2. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.3. Italy Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20. Spain Gene Therapy For Inherited Genetic Disorders Market

20.1. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.2. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.3. Spain Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market

21.1. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market Overview
21.2. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.3. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.4. Eastern Europe Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22. Russia Gene Therapy For Inherited Genetic Disorders Market

22.1. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.2. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.3. Russia Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23. North America Gene Therapy For Inherited Genetic Disorders Market

23.1. North America Gene Therapy For Inherited Genetic Disorders Market Overview
23.2. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.3. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.4. North America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24. USA Gene Therapy For Inherited Genetic Disorders Market

24.1. USA Gene Therapy For Inherited Genetic Disorders Market Overview
24.2. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.3. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.4. USA Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25. Canada Gene Therapy For Inherited Genetic Disorders Market

25.1. Canada Gene Therapy For Inherited Genetic Disorders Market Overview
25.2. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.3. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.4. Canada Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26. South America Gene Therapy For Inherited Genetic Disorders Market

26.1. South America Gene Therapy For Inherited Genetic Disorders Market Overview
26.2. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.3. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.4. South America Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27. Brazil Gene Therapy For Inherited Genetic Disorders Market

27.1. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.2. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.3. Brazil Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28. Middle East Gene Therapy For Inherited Genetic Disorders Market

28.1. Middle East Gene Therapy For Inherited Genetic Disorders Market Overview
28.2. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.3. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.4. Middle East Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29. Africa Gene Therapy For Inherited Genetic Disorders Market

29.1. Africa Gene Therapy For Inherited Genetic Disorders Market Overview
29.2. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.3. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.4. Africa Gene Therapy For Inherited Genetic Disorders Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

30. Gene Therapy For Inherited Genetic Disorders Market Competitive Landscape And Company Profiles

30.1. Gene Therapy For Inherited Genetic Disorders Market Competitive Landscape
30.2. Gene Therapy For Inherited Genetic Disorders Market Company Profiles
- 30.2.1. Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis
- 30.2.2. Novartis AG Overview, Products and Services, Strategy and Financial Analysis
- 30.2.3. Astellas Pharma Inc. Overview, Products and Services, Strategy and Financial Analysis
- 30.2.4. Vertex Pharmaceuticals Incorporated Overview, Products and Services, Strategy and Financial Analysis
- 30.2.5. Genentech Overview, Products and Services, Strategy and Financial Analysis

31. Gene Therapy For Inherited Genetic Disorders Market Other Major And Innovative Companies

31.1. Biomarin Pharmaceutical Inc
31.2. Sarepta Therapeutics Inc.
31.3. Krystal Biotech Inc.
31.4. Rocket Pharmaceuticals Inc.
31.5. Sangamo Therapeutics Inc.
31.6. REGENXBIO Inc.
31.7. Passage Bio Inc.
31.8. Voyager Therapeutics Inc.
31.9. Generation Bio Co.
31.10. Avrobio Inc
31.11. Editas Medicine Inc.
31.12. MeiraGTx Holdings Plc
31.13. uniQure N.V.
31.14. Intellia Therapeutics Inc.
31.15. Bluebird Bio Inc

32. Global Gene Therapy For Inherited Genetic Disorders Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Gene Therapy For Inherited Genetic Disorders Market

34. Recent Developments In The Gene Therapy For Inherited Genetic Disorders Market

35. Gene Therapy For Inherited Genetic Disorders Market High Potential Countries, Segments and Strategies

35.1 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Countries Offering Most New Opportunities
35.2 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Segments Offering Most New Opportunities
35.3 Gene Therapy For Inherited Genetic Disorders Market In 2029 - Growth Strategies
- 35.3.1 Market Trend Based Strategies
- 35.3.2 Competitor Strategies

36. Appendix

36.1. Abbreviations
36.2. Currencies
36.3. Historic And Forecast Inflation Rates
36.4. Research Inquiries
36.5. The Business Research Company
36.6. Copyright And Disclaimer