Global Morquio Syndrome Drug Market, By Product Type, By Treatment, By Disease Type, By Distribution Channel, By Geography

PUBLISHED: January 17, 2024

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Description

Global morquio syndrome (MPS-IV) drug market size is expected to reach US$ 4.3 Mn by 2031 from US$ 1.9 Mn in 2024, exhibiting a compound annual growth rate (CAGR) of 12.4% during the forecast period.

Report Coverage		Report Details
Base Year:	2023	Market Size in 2023/2024:	US$ 1.9 Mn
Historical Data for:	2019 to 2023	Forecast Period:	2024-2031
Forecast Period 2023/2024 to 2030/2031 CAGR:	12.40%	2030/2031 Value Projection:	US$ 4.3 Mn

Figure 1. Global Morquio Syndrome (MPS-IV) Drug Market Share (%), By Region, 2024

Global Morquio Syndrome Drug Market - IMG1

Mucopolysaccharidosis type IV (MPS IV) is a rare disease in which the body is missing or does not have enough of an enzyme needed to break down long chains of sugar molecules. These chains of molecules are called glycosaminoglycans (formerly called mucopolysaccharides). It is caused by a deficiency in the enzymes N-acetylgalactosamine-6-sulfatase (GALNS) or beta-galactosidase which is responsible for breaking down keratan sulfate and chondroitin sulfate. The accumulation of these sugars in cells, tissues, and organs can lead to skeletal dysplasia, short stature, joint abnormalities, and respiratory issues like airway obstruction, heart defects, hearing loss, and corneal opacity. There is no cure for MPS-IV and the treatment options are limited to symptom management. However, enzyme replacement therapy (ERT) and hematopoietic stem cell transplant (HSCT) have shown some success in management of symptoms and improvement in quality of life for patients. MPS IV is an inherited disorder. This means, it is typically passed down through families. If both parents carry a nonworking copy of a gene that is related to this condition, each of their children has a 25% (1 in 4) chance of developing the disease. This is called an autosomal recessive trait.

Market Dynamics:

Global morquio syndrome (MPS-IV) drug market is primarily driven by the rising prevalence of this rare genetic disorder, growing awareness about available treatment options and strong pipeline drugs with novel mechanisms of action. However, high cost of therapy due to rarity of disease as well as challenges that are associated with production of recombinant enzymes are some of the factors restraining the market growth. Nonetheless, development of improved treatment modalities, increasing research funding for rare diseases and orphan drug designation providing market exclusivity offers lucrative opportunities for the key market players in this market.

Key features of the study:

This report provides in-depth analysis of the global morquio syndrome (MPS-IV) drug market, and provides market size (US$ Mn) and compound annual growth rate (CAGR %) for the forecast period (2024-2031), considering 2023 as the base year
It elucidates potential revenue opportunities across different segments and explains attractive investment proposition matrices for this market
This study also provides key insights about market drivers, restraints, opportunities, new product launches or approval, market trends, regional outlook, and competitive strategies adopted by key players
It profiles key players in the global morquio syndrome (MPS-IV) drug market based on the following parameters - company highlights, products portfolio, key highlights, financial performance, and strategies - Key companies covered as a part of this study include BioMarin Pharmaceutical Inc., Takeda Pharmaceutical Company Limited., Pfizer Inc., Sanofi, Novo Nordisk A/S, Concert Pharmaceuticals, Inc., Alexion Pharmaceuticals Inc., Novartis AG, Amgen Inc., Sangamo Therapeutics, and JCR Pharmaceuticals Co., Ltd.
Insights from this report would allow marketers and the management authorities of the companies to make informed decisions regarding their future product launches, type up-gradation, market expansion, and marketing tactics
The global morquio syndrome (MPS-IV) drug market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts
Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the global morquio syndrome (MPS-IV) drug market

Detailed Segmentation:

Global Morquio Syndrome (MPS-IV) Drug Market, By Product Type
- Solid Dosage Form
- Tablets
- Capsules
- Liquid Dosage Form
- Injectable
- Others
Global Morquio Syndrome (MPS-IV) Drug Market, By Treatment
- Enzyme Replacement Therapy
- Hematopoietic Stem Cell Therapy
- Gene Therapy
- Others
Global Morquio Syndrome (MPS-IV) Drug Market, By Disease Type
- Morquio A
- Morquio B
Global Morquio Syndrome (MPS-IV) Drug Market, By Distribution Channel
- Hospital Pharmacies
- Online Pharmacies
- Retail Pharmacies
Global Morquio Syndrome (MPS-IV) Drug Market, By Region
- North America
- Europe
- Asia Pacific
- Latin America
- Middle East & Africa
Top Companies in the Global Morquio Syndrome (MPS-IV) Drug Market:
- BioMarin Pharmaceutical Inc.
- Takeda Pharmaceutical Company Limited.
- Pfizer Inc.
- Sanofi
- Novo Nordisk A/S
- Concert Pharmaceuticals, Inc.
- Alexion Pharmaceuticals Inc.
- Novartis AG
- Amgen Inc.
- Sangamo Therapeutics
- JCR Pharmaceuticals Co., Ltd.

Product Code: CMI6563

1. Research Objectives and Assumptions

Research Objectives
Assumptions
Abbreviations

2. Market Purview

Report Description
- Market Definition and Scope
Executive Summary
- Market Snippet, By Product Type
- Market Snippet, By Treatment
- Market Snippet, By Disease Type
- Market Snippet, By Distribution Channel
- Market Snippet, By Region
Coherent Opportunity Map (COM)

3. Market Dynamics, Regulations, and Trends Analysis

Market Dynamics
- Increasing Launch of Awareness Campaigns
- Lack of skilled healthcare professionals
- Rising healthcare expenditure
Key Highlights
Regulatory Scenario
Recent Trends
PEST Analysis
PORTER's Analysis
Product Launches
Mergers, Acquisitions, and Collaborations

4. Global Morquio Syndrome (MPS-IV) Drug Market - Impact of Coronavirus (COVID-19) Pandemic

COVID-19 Epidemiology
Supply Side and Demand Side Analysis
Economic Impact

5. Global Morquio Syndrome (MPS-IV) Drug Market, By Product Type, 2019-2031, (US$ Mn)

Introduction
Market Share Analysis, 2024 and 2031 (%)
Y-o-Y Growth Analysis, 2020 - 2031
Segment Trends
Solid Dosage Form
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Tablets
Capsules
Liquid Dosage Form
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Injectable
Others

6. Global Morquio Syndrome (MPS-IV) Drug Market, By Treatment, 2019-2031, (US$ Mn)

Introduction
Market Share Analysis, 2024 and 2031 (%)
Y-o-Y Growth Analysis, 2020 - 2031
Segment Trends
Enzyme Replacement Therapy
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Hematopoietic Stem Cell Therapy
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Gene Therapy
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Others
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)

7. Global Morquio Syndrome (MPS-IV) Drug Market, By Disease Type, 2019-2031, (US$ Mn)

Introduction
Market Share Analysis, 2024 and 2031 (%)
Y-o-Y Growth Analysis, 2020 - 2031
Segment Trends
Morquio A
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Morquio B
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)

8. Global Morquio Syndrome (MPS-IV) Drug Market, By Distribution Channel, 2019-2031, (US$ Mn)

Introduction
Market Share Analysis, 2024 and 2031 (%)
Y-o-Y Growth Analysis, 2020 - 2031
Segment Trends
Hospital Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Online Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)
Retail Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2019-2031,(US$ Mn)

9. Global Morquio Syndrome (MPS-IV) Drug Market, By Region, 2019-2031, (US$ Mn)

Introduction
Market Share Analysis, By Region, 2024 and 2031 (%)
Y-o-Y Growth Analysis, For Region, 2020 -2031
Country Trends
North America
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2019-2031,(US$ Mn)
U.S.
Canada
Europe
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2019-2031,(US$ Mn)
Germany
U.K.
Spain
France
Italy
Russia
Rest of Europe
Asia Pacific
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2019-2031,(US$ Mn)
China
India
Japan
Australia
South Korea
ASEAN
Rest of Asia Pacific
Latin America
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2019-2031,(US$ Mn)
Brazil
Argentina
Mexico
Rest of Latin America
Middle East
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2019-2031,(US$ Mn)
GCC Countries
Israel
Rest of Middle East
Africa
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Product Type, 2019-2031,(US$
Market Size and Forecast, and Y-o-Y Growth, By Treatment, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2019-2031,(US$ Mn)
Market Size and Forecast, and Y-o-Y Growth, By Country/Region, 2019-2031,(US$ Mn)
North Africa
Central Africa
South Africa